An international working group met on March 25 in the UK to discuss clinical measures that could be used to establish the efficacy of drugs in the treatment of Ataxia of Charlevoix-Saguenay. This special meeting was held within the framework of the International Meeting for Research on ataxia organized by several associations dedicated to promoting research in ataxia including: AtaxiaUK, Ataxia Ireland, and FARA GOFAR Italian Association. The meeting was chaired by Cynthia Gagnon, Bernard Brais and Paola Giunti the National Hospital for Neurology and Neurosurgery in London. It brought together clinicians and researchers from France, Italy, Belgium, England and Germany.
The work of Dr. Gagnon’s team was the starting point for discussion. This helped to establish more concrete goals that will lead to greater international collaboration to accelerate the transition from scientific discovery to clinical trials