The goal of their project is to develop a new approach that could directly correct the genetic error responsible for the disease. The researchers will use a recent technology called Prime Editing, which acts somewhat like a spell checker for DNA. Its role is to replace an incorrect letter in the genetic code.
Grant: $100,000
Duration: One year
Dr. Jacques-P. Tremblay
Professor
Department of Molecular Medicine
Faculty of Medicine, Université Laval
Quebec City, Quebec, Canada
Contact: jacques-p.tremblay@fmed.ulaval.ca